1. At my last count, there are at least a half dozen completely separate "precision medicine" projects for people with ALS.
a. Has anyone actually established protocols and shared data between any of these silos?
b. Is anyone concerned about the duplication of resources and infrastructure?
2. Are there any specific novel clinical trial design features that you expect to see implemented in the next 12 months as a result of the Airlie House guidelines or the ALSA FDA draft guidance work?
Information about "Ask the Experts" can be found at
We are grateful for the live stream this year and hope that more of the symposium activities will be live streamed in the future for those who are interested in the newest and best science but cannot travel.